RARECast
A podcast by RARECast - Joi
548 Episoade
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A Heart Attack that Led to a Rare Disease Diagnosis
Publicat: 30.01.2025 -
Targeting Rare Liver Diseases with Gene Editing Therapies
Publicat: 23.01.2025 -
Using AI to De-Risk Rare Disease Drug Development
Publicat: 16.01.2025 -
Addressing a Growing Demand for Plasma-Derived Therapies
Publicat: 09.01.2025 -
Empowering Patients with Data to Drive Drug Development
Publicat: 02.01.2025 -
How Advocates Are Advancing a Treatment for an Ultra-Rare Disease
Publicat: 26.12.2024 -
Engineering B Cells to Produce Therapeutic Proteins
Publicat: 19.12.2024 -
A Pipeline Win as BridgeBio Learns to Balance Theory with Practice
Publicat: 12.12.2024 -
Considering What It Will Take for Payers to Embrace Advances in Sequencing
Publicat: 05.12.2024 -
Finding Strength
Publicat: 27.11.2024 -
A Non-Profit Works to Advance a DMD Gene Therapy
Publicat: 21.11.2024 -
Accepting What We Can’t Understand
Publicat: 14.11.2024 -
A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Publicat: 07.11.2024 -
Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Publicat: 31.10.2024 -
Scaling N-of-1 Therapies to Viability
Publicat: 24.10.2024 -
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Publicat: 17.10.2024 -
How One Woman Climbed from Patient to Advocate
Publicat: 10.10.2024 -
Shortening the Diagnostic Odyssey
Publicat: 03.10.2024 -
Making Exomes More Revealing
Publicat: 26.09.2024 -
How One Patient Organization Catalyzed Drug Development
Publicat: 19.09.2024
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
