548 Episoade

  1. Overcoming a Delivery Challenge of Retinal Gene Therapies

    Publicat: 19.06.2025

  2. A Gene Editing First Augurs an Era of Bespoke Therapies

    Publicat: 12.06.2025

  3. How One Patient Organization Drives Drug Development

    Publicat: 05.06.2025

  4. Using CRISPR to Modulate Gene Expression

    Publicat: 29.05.2025

  5. Satisfying the Hunger for a Prader-Willi Therapy

    Publicat: 22.05.2025

  6. How an Academic Medical Center Helped Change the Landscape for a Rare Disease

    Publicat: 15.05.2025

  7. Improving Outcomes for People with a Set of Rare Cancers

    Publicat: 08.05.2025

  8. An Effort to Build a Better DMD Gene Therapy

    Publicat: 02.05.2025

  9. A Once-Failed Pain Therapy Shows Potential in a Neurodevelopmental Disorder

    Publicat: 24.04.2025

  10. Advancing a Cutting-Edge Therapy for a Rare, Childhood Cancer

    Publicat: 17.04.2025

  11. Learning to Take His Vitamins

    Publicat: 10.04.2025

  12. The First Treatment for a Rare Neurodegenerative Condition Awaits FDA Approval

    Publicat: 03.04.2025

  13. Engineering Skin Bacteria to Be Live Biotherapeutics

    Publicat: 27.03.2025

  14. Seeing the Gene and Cell Therapy Translational Divide as an Opportunity

    Publicat: 20.03.2025

  15. My Mother, Myself, and ALS

    Publicat: 13.03.2025

  16. From Immovable Object to Advocacy Force

    Publicat: 06.03.2025

  17. A Rapid and Scalable Approach for Screening Personalized ASOs

    Publicat: 27.02.2025

  18. Addressing the Disease Mechanism of a Rare Kidney Disease

    Publicat: 20.02.2025

  19. The Mother of a Son with SCD, Applies Direct Experience to Her Clinical Trials Work

    Publicat: 13.02.2025

  20. A First for Rett Syndrome with More in the Pipeline

    Publicat: 06.02.2025

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RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

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